Gene Therapy
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Team Uses AI + Quantum Computing to Design Molecules for ‘Undruggable’ KRAS Cancer Protein
Read more: Team Uses AI + Quantum Computing to Design Molecules for ‘Undruggable’ KRAS Cancer ProteinThe researchers combined quantum computing and generative AI with classical computing methods to create molecules targeting a cancer-driving protein called KRAS.
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FDA Raises Red Flags on Sarepta’s Duchenne Gene Therapy for Heart Risks
Read more: FDA Raises Red Flags on Sarepta’s Duchenne Gene Therapy for Heart RisksRisk of ‘acute, serious, and life-threatening’ heart inflammation is now on the label of Sarepta’s gene therapy for Duchenne muscular dystrophy. What happens next?
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Personalized Longevity Plans: Epigenetics Meets Everyday Health
Read more: Personalized Longevity Plans: Epigenetics Meets Everyday Health“Clinics now use gene sequencing, biomarker profiling, and senolytic drugs to design custom plans, targeting the biology of aging for healthy lifespans.”
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First-Ever Personalized CRISPR Treatment Delivered
Read more: First-Ever Personalized CRISPR Treatment Delivered“In 2025, a bespoke in vivo CRISPR therapy was developed for an infant in just six months—signaling a new era of on-demand, patient-specific gene editing.”
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AMT-130: Gene Therapy Breakthrough for Huntington’s Disease
Read more: AMT-130: Gene Therapy Breakthrough for Huntington’s Disease“A revolutionary treatment that halts the body’s production of toxic huntington’s protein shows promise in dramatically slowing disease progression.”
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Revolutionizing Medicine with AI and Gene Therapy
Read more: Revolutionizing Medicine with AI and Gene TherapyArtificial intelligence algorithms have revolutionized medical diagnostics, allowing for early detection of diseases like cancer with unprecedented accuracy.
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CRISPR Therapeutics and Gene Editing
Read more: CRISPR Therapeutics and Gene EditingNew CRISPR-Cas9 based treatments, like Casgevy, received FDA approval and inspired numerous trials addressing genetic disorders, cancer, and autoimmune diseases. Advances in base and prime editing have shifted the focus from symptom management to potentially curative therapies, transforming drug discovery and personalized medicine.